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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
47
Publications avec texte intégral
Open Access
73 %
Mots clés
Cardiomyopathie
Autophagy
NAD+
Molecular docking
Génomique
Male
Muscles/physiopathology
Mitochondrial fission
Cell homeostasis
Becker BMD muscular dystrophy
DMO
Dystrophin central domain
Dystrophin-EGFP
Myotendinous junction
Dynamin 2
CaVβs
Long QT
Antisense oligonucleotides
Epigenetics
LncRNA
NNOS
Human Umbilical Vein Endothelial Cells
Energy Metabolism/drug effects
Muscular Atrophy
Dystrophie Musculaire de Duchenne DMD
Cachexia
Metabolism
Animals
CTNNB1
Mice
Gene expression
Skeletal muscle
Muscular dystrophy
Myogenesis
Ex-vivo
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Calcium
Cells
Allele‐specific silencing therapy
Clinical trials
Genomic
Exon skipping
Cardiomyopathy
Cell Line
DMD
Base Sequence
Calcium Channels
Gene Expression Regulation/drug effects
BMD
Cultured
Duchenne muscular dystrophy
LncARN
Mdx mouse
MES
L-Type
Cell Biology
Dystrophin
Liver
LKB1
Muscle
Multi resolution modeling
Becker muscular dystrophy
Gene modifiers
MiARN
CD38
Dystrophie musculaire de Becker
Multiresolution modeling
Dystrophie Musculaire de Becker BMD
Immunoglobulin Fc Fragments/pharmacology
Multi exon skipping
Knockout
Dystrophine
CaV subunits
Inhibitors
Animal/physiopathology
Dystrophy
Hepatocellular carcinoma
Inbred mdx
Becker muscular dystrophy BMD
Long noncoding RNA
Molecular Sequence Data
Humans
Inbred C57BL
Morphogenesis
Modificateurs de gènes
Invivo
Activin Receptors
Duchenne DMD dystrophy
Hear
Muscular Dystrophy
Duchenne muscular dystrophy DMD
Drp1
DHPR α1S
Muscle development
Delivery
Muscle Strength
Homeostasis
Muscle Biology
Diseases
Centronuclear myopathy