index - Thérapie génique pour la DMD & physiopathologie du muscle squelettique

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Cardiomyopathie Autophagy NAD+ Molecular docking Génomique Male Muscles/physiopathology Mitochondrial fission Cell homeostasis Becker BMD muscular dystrophy DMO Dystrophin central domain Dystrophin-EGFP Myotendinous junction Dynamin 2 CaVβs Long QT Antisense oligonucleotides Epigenetics LncRNA NNOS Human Umbilical Vein Endothelial Cells Energy Metabolism/drug effects Muscular Atrophy Dystrophie Musculaire de Duchenne DMD Cachexia Metabolism Animals CTNNB1 Mice Gene expression Skeletal muscle Muscular dystrophy Myogenesis Ex-vivo Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS Calcium Cells Allele‐specific silencing therapy Clinical trials Genomic Exon skipping Cardiomyopathy Cell Line DMD Base Sequence Calcium Channels Gene Expression Regulation/drug effects BMD Cultured Duchenne muscular dystrophy LncARN Mdx mouse MES L-Type Cell Biology Dystrophin Liver LKB1 Muscle Multi resolution modeling Becker muscular dystrophy Gene modifiers MiARN CD38 Dystrophie musculaire de Becker Multiresolution modeling Dystrophie Musculaire de Becker BMD Immunoglobulin Fc Fragments/pharmacology Multi exon skipping Knockout Dystrophine CaV subunits Inhibitors Animal/physiopathology Dystrophy Hepatocellular carcinoma Inbred mdx Becker muscular dystrophy BMD Long noncoding RNA Molecular Sequence Data Humans Inbred C57BL Morphogenesis Modificateurs de gènes Invivo Activin Receptors Duchenne DMD dystrophy Hear Muscular Dystrophy Duchenne muscular dystrophy DMD Drp1 DHPR α1S Muscle development Delivery Muscle Strength Homeostasis Muscle Biology Diseases Centronuclear myopathy